5
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| breast cancer | azeliragon | Orphan Designation | - |
| familial adenomatous polyposis 1 | azeliragon | Orphan Designation | - |
| glioblastoma | azeliragon | Orphan Designation | - |
| glioma susceptibility 1 | combination of disulfiram and copper gluconate | Orphan Designation | - |
| malignant pancreatic neoplasm | azeliragon | Orphan Designation | - |
| plasma cell myeloma | Disulfiram and Copper | Orphan Designation | - |