3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute myeloid leukemia | CRISPR-edited allogeneic CLL-1-targeted CAR-T Cells | Orphan Designation | - |
| follicular lymphoma | Edited allogeneic chimeric antigen receptor T Cells (CAR-T) | Orphan Designation | - |
| folliculotropic mycosis fungoides | Edited allogeneic chimeric antigen receptor T Cells (CAR-T) | Orphan Designation | - |
| lymphoma, non-Hodgkin, familial | Edited allogeneic chimeric antigen receptor T Cells (CAR-T) | Orphan Designation | - |
| plasma cell myeloma | Allogeneic CAR-T cells that is engineered to express a CAR targeting the B cell maturation antigen (BCMA) | Orphan Designation | - |