1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Chagas disease | benznidazole | Orphan Designation | - |
| Huntington disease | benznidazole | Orphan Designation | - |
| breast fibrocystic disease | benznidazole | Orphan Designation | - |
| rheumatic disease of mitral valve | benznidazole | Orphan Designation | - |
| short stature-webbed neck-heart disease syndrome | benznidazole | Orphan Designation | - |