Skip to main content
Diseases
Companies
News
Policy
About
Resources
Build with
KISHO
Sign In
Sign Up
Open menu
Kisho
ChemoCentryx, Inc. — Rare Disease Pipeline | Kisho | Kisho
ChemoCentryx, Inc.
Other
4
Orphan Designations
1
FDA Approvals
16
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
Chilton-Okur-Chung neurodevelopmental syndrome
Tavneos
Orphan Designation
-
Okur-Chung neurodevelopmental syndrome
Tavneos
Orphan Designation
-
Pan-Chung-Bellen syndrome
Tavneos
Orphan Designation
-
adult neuronal ceroid lipofuscinosis
Tavneos
Orphan Designation
-
adult pleomorphic rhabdomyosarcoma
Tavneos
Orphan Designation
-
adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia
Tavneos
Orphan Designation
-
adult-onset proximal spinal muscular atrophy, autosomal dominant
Tavneos
Orphan Designation
-
anti-neutrophil cytoplasmic antibody-associated vasculitis
Tavneos
Orphan Designation
-
atypical hemolytic-uremic syndrome
avacopan
Orphan Designation
-
eosinophilic granulomatosis with polyangiitis
Tavneos
Orphan Designation
-
focal segmental glomerulosclerosis
4-Chloro-N-[5-methyl-2-(7H-pyrrolo[2,3-d]pyrimidin-4-ylcarbonyl)-3-pyridinyl]-3-(trifluoromethyl)benzenesulfonamide, sodium salt
Orphan Designation
-
microscopic polyangiitis
Tavneos
Orphan Designation
-
non-immunoglobulin-mediated membranoproliferative glomerulonephritis
avacopan
Orphan Designation
-
pauci-immune glomerulonephritis with ANCA
Tavneos
Orphan Designation
-
pauci-immune glomerulonephritis without ANCA
Tavneos
Orphan Designation
-
primary adult heart tumor
Tavneos
Orphan Designation
-
← Back to Companies