1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| chromosome 15q24 deletion syndrome | Glyceol | Orphan Designation | - |
| infantile hypophosphatasia | Glyceol | Orphan Designation | - |
| neurodevelopmental disorder with intracranial hemorrhage, seizures, and spasticity | Glyceol | Orphan Designation | - |