2
Orphan Designations
1
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| adult neuronal ceroid lipofuscinosis | Lymphir | Orphan Designation | - |
| adult pleomorphic rhabdomyosarcoma | Lymphir | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | Lymphir | Orphan Designation | - |
| adult-onset proximal spinal muscular atrophy, autosomal dominant | Lymphir | Orphan Designation | - |
| enteropathy-associated T-cell lymphoma | denileukin diftitox | Orphan Designation | - |
| mature T-cell and NK-cell non-Hodgkin lymphoma | denileukin diftitox | Orphan Designation | - |
| peripheral T-cell lymphoma, not otherwise specified | denileukin diftitox | Orphan Designation | - |
| primary adult heart tumor | Lymphir | Orphan Designation | - |
| primary cutaneous T-cell non-Hodgkin lymphoma | Lymphir | Orphan Designation | - |