4
Orphan Designations
1
FDA Approvals
13
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| CD4+/CD56+ hematodermic neoplasm | afamelanotide | Orphan Designation | - |
| Hailey-Hailey disease | afamelanotide | Orphan Designation | - |
| autosomal erythropoietic protoporphyria | SCENESSE® | Orphan Designation | - |
| cutaneous porphyria | SCENESSE® | Orphan Designation | - |
| erythropoietic protoporphyria | SCENESSE® | Orphan Designation | - |
| neutropenia, chronic familial | afamelanotide | Orphan Designation | - |
| primary cutaneous lymphoma | afamelanotide | Orphan Designation | - |
| protoporphyria, erythropoietic, 1 | SCENESSE® | Orphan Designation | - |
| recessive dystrophic epidermolysis bullosa | afamelanotide | Orphan Designation | - |
| seizures, benign familial neonatal, 2 | afamelanotide | Orphan Designation | - |
| solar urticaria | afamelanotide | Orphan Designation | - |
| variegate porphyria | afamelanotide | Orphan Designation | - |
| xeroderma pigmentosum variant type | afamelanotide | Orphan Designation | - |