1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Hermansky-Pudlak syndrome 7 | Human recombinant factor VIIa variant (P10Q, K32E, T106N, V253N), desialylated | Orphan Designation | - |
| bleeding disorder, platelet-type, 25 | Human recombinant factor VIIa variant (P10Q, K32E, T106N, V253N), desialylated | Orphan Designation | - |
| thrombocytopenia 7 | Human recombinant factor VIIa variant (P10Q, K32E, T106N, V253N), desialylated | Orphan Designation | - |