3
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| chronic liver failure | emricasan | Orphan Designation | - |
| liver and intrahepatic bile duct neoplasm | emricasan | Orphan Designation | - |
| liver angiosarcoma | emricasan | Orphan Designation | - |
| liver cancer | emricasan | Orphan Designation | - |
| liver failure | emricasan | Orphan Designation | - |
| liver fibrocystic disease and polydactyly | emricasan | Orphan Designation | - |
| multiple organ dysfunction syndrome | 4-[[[4-(4-Chlorophenoxy)phenyl]sulfonyl]-methyl] tetrahydro-N-hydroxy-2H-pyran-4-carboxamide | Orphan Designation | - |
| primary organ-specific lymphoma | 4-[[[4-(4-Chlorophenoxy)phenyl]sulfonyl]-methyl] tetrahydro-N-hydroxy-2H-pyran-4-carboxamide | Orphan Designation | - |
| sclerosing cholangitis | (S)-3-((S)-2-(2-((2,6-difluorophenyl)amino)-2-oxoacetamido)propanamido-4-oxo-5-(2,3,5,6-tetrafluorophenoxy)pentanoic acid | Orphan Designation | - |
| sensory organ benign neoplasm | 4-[[[4-(4-Chlorophenoxy)phenyl]sulfonyl]-methyl] tetrahydro-N-hydroxy-2H-pyran-4-carboxamide | Orphan Designation | - |