2
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Loeys-Dietz syndrome 4 | hyaluronic acid | Orphan Designation | - |
| Meier-Gorlin syndrome 4 | hyaluronic acid | Orphan Designation | - |
| alpha 1-antitrypsin deficiency | hyaluronic acid | Orphan Designation | - |
| drug- or toxin-induced pulmonary arterial hypertension | Ventavis | Orphan Designation | - |
| familial pulmonary arterial hypertension leucopenia and atrial septal defect | Ventavis | Orphan Designation | - |
| heritable pulmonary arterial hypertension | Ventavis | Orphan Designation | - |
| idiopathic pulmonary arterial hypertension | Ventavis | Orphan Designation | - |
| pulmonary arterial hypertension | Ventavis | Orphan Designation | - |