2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| cerebrooculofacioskeletal syndrome 1 | Alpha1-proteinase inhibitor (human) | Orphan Designation | - |
| microcephaly 13, primary, autosomal recessive | Alpha1-proteinase inhibitor (human) | Orphan Designation | - |
| microcephaly-capillary malformation syndrome | Alpha1-proteinase inhibitor (human) | Orphan Designation | - |
| systemic sclerosis | Immune Globulin (Human) | Orphan Designation | - |