1
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Combarros Calleja Leno syndrome | a peptidomimetic protein peptide with sequence H-Gly-Arg-Arg-Ala-Ala-Pro-Gly-Arg-Aib-Gly-Gly-NH2 | Orphan Designation | - |
| Lennox-Gastaut syndrome | a peptidomimetic protein peptide with sequence H-Gly-Arg-Arg-Ala-Ala-Pro-Gly-Arg-Aib-Gly-Gly-NH2 | Orphan Designation | - |