2
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Opitz G/BBB syndrome | Sucralfate suspension | Orphan Designation | - |
| aphthous stomatitis | Sucralfate suspension | Orphan Designation | - |
| congenital disorder of deglycosylation 1 | Sucralfate suspension | Orphan Designation | - |
| lip and oral cavity carcinoma | Sucralfate suspension | Orphan Designation | - |
| mucocutaneous ulceration, chronic | Sucralfate suspension | Orphan Designation | - |
| oral cavity cancer | Sucralfate suspension | Orphan Designation | - |
| oral mucosa leukoplakia | Sucralfate suspension | Orphan Designation | - |
| spinal muscular atrophy with congenital bone fractures 1 | Sucralfate suspension | Orphan Designation | - |
| spinal muscular atrophy with congenital bone fractures 2 | Sucralfate suspension | Orphan Designation | - |