1
Orphan Designations
2
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kleefstra syndrome 1 | Ojemda | Orphan Designation | - |
| Shashi-Pena syndrome | Ojemda | Orphan Designation | - |
| chromosome 5q12 deletion syndrome | Ojemda | Orphan Designation | - |
| malignant glioma | Ojemda | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | Ojemda | Orphan Designation | - |