3
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Beckwith-Wiedemann syndrome | vapreotide | Orphan Designation | - |
| Johanson-Blizzard syndrome | vapreotide | Orphan Designation | - |
| Martinez-Frias syndrome | vapreotide | Orphan Designation | - |
| early-onset familial hypoaldosteronism | vapreotide | Orphan Designation | - |
| early-onset generalized limb-onset dystonia | vapreotide | Orphan Designation | - |
| early-onset parkinsonism-intellectual disability syndrome | vapreotide | Orphan Designation | - |
| fanconi anemia, complementation group 10 | vapreotide | Orphan Designation | - |
| gastrointestinal stromal tumor | vapreotide | Orphan Designation | - |
| gastrointestinal tuberculosis | vapreotide | Orphan Designation | - |
| ovarian cancer | Oxaliplatin | Orphan Designation | - |