Skip to main content
Diseases
Companies
News
Policy
About
Resources
Build with
KISHO
Sign In
Sign Up
Open menu
Kisho
Deciphera Pharmaceuticals, LLC — Rare Disease Pipeline | Kisho | Kisho
Deciphera Pharmaceuticals, LLC
Other
5
Orphan Designations
2
FDA Approvals
14
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
B-lymphoblastic leukemia/lymphoma with t(9;22)(q34.1;q11.2)
Rebastinib
Orphan Designation
-
Carney-Stratakis syndrome
Ripretinib
Orphan Designation
-
IDH-mutant anaplastic astrocytoma
KIT and PDGFR inhibitor
Orphan Designation
-
IDH-wildtype anaplastic astrocytoma
KIT and PDGFR inhibitor
Orphan Designation
-
Philadelphia-positive myelogenous leukemia
Rebastinib
Orphan Designation
-
adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia
Ripretinib
Orphan Designation
-
anaplastic astrocytoma
KIT and PDGFR inhibitor
Orphan Designation
-
chronic myelogenous leukemia, BCR-ABL1 positive
Rebastinib
Orphan Designation
-
colorectal gastrointestinal stromal tumor
Ripretinib
Orphan Designation
-
gastrointestinal stromal tumor
Ripretinib
Orphan Designation
-
glioma susceptibility 1
KIT and PDGFR inhibitor
altiratinib
Orphan Designation
-
pheochromocytoma/paraganglioma syndrome 4
Ripretinib
Orphan Designation
-
primary adult heart tumor
Ripretinib
Orphan Designation
-
primary central nervous system lymphoma
tirabrutinib
Orphan Designation
-
← Back to Companies