1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| dermatomyositis | (R)-N-(2-fluorobenzyl)-2,4-dimethyl-1-(oxetan-3-ylmethyl)-3-oxo- 1,2,3,4-tetrahydroquinoxaline-6-carboxamide | Orphan Designation | - |
| mevalonic aciduria | (R)-N-(2-fluorobenzyl)-2,4-dimethyl-1-(oxetan-3-ylmethyl)-3-oxo- 1,2,3,4-tetrahydroquinoxaline-6-carboxamide | Orphan Designation | - |
| nut midline carcinoma | (R)-N-(2-fluorobenzyl)-2,4-dimethyl-1-(oxetan-3-ylmethyl)-3-oxo- 1,2,3,4-tetrahydroquinoxaline-6-carboxamide | Orphan Designation | - |