1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Renpenning syndrome | allogeniec Human Pancreatic Islets of Langerhans | Orphan Designation | - |
| brittle cornea syndrome | allogeniec Human Pancreatic Islets of Langerhans | Orphan Designation | - |
| orofaciodigital syndrome I | allogeniec Human Pancreatic Islets of Langerhans | Orphan Designation | - |