1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Wolcott-Rallison syndrome | Recombinant human glutamic acid decarboxylase 65KDa isoform | Orphan Designation | - |
| immune dysregulation-polyendocrinopathy-enteropathy-X-linked syndrome | Recombinant human glutamic acid decarboxylase 65KDa isoform | Orphan Designation | - |
| odontochondrodysplasia 2 with hearing loss and diabetes | Recombinant human glutamic acid decarboxylase 65KDa isoform | Orphan Designation | - |