4
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute graft versus host disease | reparixin | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | reparixin | Orphan Designation | - |
| chronic graft versus host disease | reparixin | Orphan Designation | - |
| delayed membranous cranial ossification | reparixin | Orphan Designation | - |
| delayed puberty, self-limited | reparixin | Orphan Designation | - |
| graft versus host disease | reparixin | Orphan Designation | - |
| neurotrophic keratopathy | Oxervate | Orphan Designation | - |
| retinitis pigmentosa | recombinant human nerve growth factor | Orphan Designation | - |