2
Orphan Designations
0 approved, 2 designated
0
FDA Approvals
0
Active Trials
200 recruiting
3
Rare Diseases
across 3 areas
0
News (30d)
Quiet
Dr. Noah Biotech, Inc. is a company with 2 orphan drug designations across 3 rare diseases. 5 active policy bills affect their portfolio.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| Becker muscular dystrophy | fixed-dosed combination of L-citrulline + allopurinol | Des.TrialAppr. |
| Duchenne muscular dystrophy | fixed-dosed combination of L-citrulline + allopurinol | Des.TrialAppr. |
| amyotrophic lateral sclerosis | Fixed-dose combination of Donepezil hydrochloride and Nebivolol hydrochloride | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
32
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
5
affecting portfolio
0% of portfolio targets high unmet need diseases
32
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
5
affecting portfolio