1
Orphan Designations
1
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Gaucher disease type III | Anthim | Orphan Designation | - |
| deafness, aminoglycoside-induced | Anthim | Orphan Designation | - |
| deafness, congenital, and adult-onset progressive leukoencephalopathy | Anthim | Orphan Designation | - |
| drug allergy | Anthim | Orphan Designation | - |
| exposure keratitis | Anthim | Orphan Designation | - |
| exposure, dental pulp | Anthim | Orphan Designation | - |