1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute flaccid myelitis | N-(9-methoxynonyl)-1-deoxynojirimycin hydrochloride | Orphan Designation | - |
| acute lymphoblastic leukemia | N-(9-methoxynonyl)-1-deoxynojirimycin hydrochloride | Orphan Designation | - |
| dengue disease | N-(9-methoxynonyl)-1-deoxynojirimycin hydrochloride | Orphan Designation | - |
| dengue shock syndrome | N-(9-methoxynonyl)-1-deoxynojirimycin hydrochloride | Orphan Designation | - |
| hereditary thrombocytopenia and hematological cancer predisposition syndrome associated with RUNX1 | N-(9-methoxynonyl)-1-deoxynojirimycin hydrochloride | Orphan Designation | - |
| primary membranoproliferative glomerulonephritis | N-(9-methoxynonyl)-1-deoxynojirimycin hydrochloride | Orphan Designation | - |