9
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute myeloid leukemia | 2-(2-phenylvinyl)-4-[-methylpiperazin-l-yl)]-6-(5-methyl-2H-pyrazol-3-yl-amino)-pyrimidine L(+) tartrate salt | Orphan Designation | - |
| adult glioblastoma | 2-methoxyestradiol | Orphan Designation | - |
| adult spinal cord glioblastoma | 2-methoxyestradiol | Orphan Designation | - |
| cutaneous neuroendocrine carcinoma | Recombinant human endostatin protein | Orphan Designation | - |
| glioblastoma | 2-methoxyestradiol | Orphan Designation | - |
| metastatic melanoma | recombinant human endostatin protein | Orphan Designation | - |
| ovarian cancer | 2-methoxyestradiol | Orphan Designation | - |
| ovarian carcinoma | 2-(2-phenylvinyl)-4-[4-methylpiperazin-l-yl)]-6-(5-methyl-2H-pyrazol-3-ylamino)-pyrimidine L(+) tartrate salt | Orphan Designation | - |
| pancreatic neuroendocrine neoplasm | Recombinant human endostatin protein | Orphan Designation | - |
| pancreatic neuroendocrine tumor | Recombinant human endostatin protein | Orphan Designation | - |
| plasma cell myeloma | 2-(2-phenylvinyl)-4-[4-methylpiperazin-l-yl)]-6-(5-methyl-2H-pyrazol-3-yl-amino)-pyrimidine L(+) tartrate saltS(-)-3-[3-amino-phthalimido]-glutaramide2-methoxyestradiol | Orphan Designation | - |