1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Johanson-Blizzard syndrome | Rethymic | Orphan Designation | - |
| congenital | Rethymic | Orphan Designation | - |
| congenital adrenal hyperplasia | Rethymic | Orphan Designation | - |
| congenital heart disease | Rethymic | Orphan Designation | - |
| immune dysregulation-polyendocrinopathy-enteropathy-X-linked syndrome | Rethymic | Orphan Designation | - |
| immune reconstitution inflammatory syndrome | Rethymic | Orphan Designation | - |