1
Orphan Designations
0 approved, 1 designated
0
FDA Approvals
1
Active Trials
182 recruiting
4
Rare Diseases
across 5 areas
0
News (30d)
Quiet
Equilibra Bioscience LLC is a company with 1 orphan drug designation across 4 rare diseases. Active clinical trials in 1 indication.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| hemophilia A | recombinant anti-human activated protein C humanized monoclonal antibody | Des.TrialAppr. |
| hemophilia A with vascular abnormality | recombinant anti-human activated protein C humanized monoclonal antibody | Des.TrialAppr. |
| hemophilia B | - | Des.TrialAppr. |
| severe hemophilia A | recombinant anti-human activated protein C humanized monoclonal antibody | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
18
overlap in 2+ diseases
0/4
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
18
overlap in 2+ diseases
0/4
candidate diseases
0
avg importance: 0
0
affecting portfolio