1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bicervical bicornuate uterus with patent cervix and vagina | autologous, engineered regulatory T-cell immunotherapy, designed to express an islet antigen-specific T cell receptor, stable Forkhead box P3 (FOXP3) protein, and a chemically induced signaling complex that promotes selective interleukin 2-pathway signaling | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | autologous, engineered regulatory T-cell immunotherapy, designed to express an islet antigen-specific T cell receptor, stable Forkhead box P3 (FOXP3) protein, and a chemically induced signaling complex that promotes selective interleukin 2-pathway signaling | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | autologous, engineered regulatory T-cell immunotherapy, designed to express an islet antigen-specific T cell receptor, stable Forkhead box P3 (FOXP3) protein, and a chemically induced signaling complex that promotes selective interleukin 2-pathway signaling | Orphan Designation | - |