1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| adult embryonal tumor with multilayered rosettes, c19mc-altered | Pretomanid | Orphan Designation | - |
| cystic fibrosis | Pretomanid | Orphan Designation | - |
| dermatomyositis | Pretomanid | Orphan Designation | - |
| nut midline carcinoma | Pretomanid | Orphan Designation | - |
| tuberculosis | Pretomanid | Orphan Designation | - |