3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute myeloid leukemia | E-selectin antagonist | Orphan Designation | - |
| osteosarcoma | dual E-selectin and C-X-C chemokine receptor Type 4 (CXCR4) antagonist that targets both E-selectin and CXCR4 | Orphan Designation | - |
| vas deferens, congenital bilateral aplasia of, X-linked | (1R,3R,4R,5S)-3-O-[2-O-benzoyl-3-O-(sodium(2S)-3-cyclohexyl-propanoate- | Orphan Designation | - |
| vas deferens, congenital unilateral aplasia of | (1R,3R,4R,5S)-3-O-[2-O-benzoyl-3-O-(sodium(2S)-3-cyclohexyl-propanoate- | Orphan Designation | - |
| vasa previa | (1R,3R,4R,5S)-3-O-[2-O-benzoyl-3-O-(sodium(2S)-3-cyclohexyl-propanoate- | Orphan Designation | - |