2
Orphan Designations
0 approved, 2 designated
0
FDA Approvals
0
Active Trials
2
Rare Diseases
across 5 areas
7
News (30d)
Trending
GSK LLC is a company with 2 orphan drug designations across 2 rare diseases. 7 news articles in the past 30 days.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| malignant glioma | niraparib | Des.TrialAppr. |
| systemic sclerosis | belimumab | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
2
overlap in 2+ diseases
0/2
candidate diseases
7
avg importance: 44
0
affecting portfolio
0% of portfolio targets high unmet need diseases
2
overlap in 2+ diseases
0/2
candidate diseases
7
avg importance: 44
0
affecting portfolio