1
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| MPI-congenital disorder of glycosylation | ATryn | Orphan Designation | - |
| PGM1-congenital disorder of glycosylation | ATryn | Orphan Designation | - |
| SRD5A3-congenital disorder of glycosylation | ATryn | Orphan Designation | - |
| advanced sleep phase syndrome 3 | ATryn | Orphan Designation | - |
| electroencephalographic peculiarity: 14 and 6 per sec. positive spike phenomenon | ATryn | Orphan Designation | - |
| hereditary antithrombin deficiency | ATryn | Orphan Designation | - |
| peripartum cardiomyopathy | ATryn | Orphan Designation | - |
| postpartum depression | ATryn | Orphan Designation | - |