3
Orphan Designations
3 approved
0
FDA Approvals
0
Active Trials
4
Rare Diseases
across 9 areas
0
News (30d)
Quiet
GW Research Ltd. is a company with 3 orphan drug designations across 4 rare diseases.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| Dravet syndrome | EPIDIOLEX | Des.TrialAppr. |
| Lennox-Gastaut syndrome | EPIDIOLEX | Des.TrialAppr. |
| febrile seizures, familial | EpidiolexEPIDIOLEX | Des.TrialAppr. |
| tuberous sclerosis | Epidiolex | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
11
overlap in 2+ diseases
0/4
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
11
overlap in 2+ diseases
0/4
candidate diseases
0
avg importance: 0
0
affecting portfolio