1
Orphan Designations
0 approved, 1 designated
0
FDA Approvals
0
Active Trials
6
Rare Diseases
across 10 areas
0
News (30d)
Quiet
Gynuity Health Projects, LLC is a company with 1 orphan drug designation across 6 rare diseases. gene therapy candidates in 1 disease.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| fetal growth restriction | misoprostol | Des.TrialAppr. |
| lethal fetal cerebrorenogenitourinary agenesis/hypoplasia syndrome | misoprostol | Des.TrialAppr. |
| neurodevelopmental disorder with dystonia and seizures | misoprostol | Des.TrialAppr. |
| pregnancy disorder with abortive outcome | misoprostol | Des.TrialAppr. |
| third branchial cleft anomaly | misoprostol | Des.TrialAppr. |
| total third-nerve palsy | misoprostol | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
0
overlap in 2+ diseases
1/6
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
0
overlap in 2+ diseases
1/6
candidate diseases
0
avg importance: 0
0
affecting portfolio