3
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| FOXG1 disorder | vepafestinib | Orphan Designation | - |
| RET fusion positive cancer | vepafestinib | Orphan Designation | - |
| acute myeloid leukemia | pracinostat | Orphan Designation | - |
| bile duct cancer | DEAE-rebeccamycin | Orphan Designation | - |
| bile duct neoplasm | DEAE-rebeccamycin | Orphan Designation | - |
| malignant tumor of extrahepatic bile duct | DEAE-rebeccamycin | Orphan Designation | - |