A pharmaceutical company engaged in developing and providing treatments for rare diseases, with 33 FDA-approved drugs and active involvement in six rare conditions, including neuroblastoma and neonatal seizures.
1
Orphan Designations
33
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| apnea of prematurity | CAFFEINE CITRATE | - | FDA Approved |
| benign idiopathic neonatal seizures | Phenobarbital Sodium | Orphan Designation | - |
| benign neonatal seizures | Phenobarbital Sodium | Orphan Designation | - |
| infective endocarditis | TYZAVAN | - | FDA Approved |
| neuroblastoma | CYCLOPHOSPHAMIDE | - | FDA Approved |
| self-limited neonatal seizures | Phenobarbital Sodium | Orphan Designation | - |