11
Orphan Designations
3
FDA Approvals
20
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| atypical hemolytic-uremic syndrome | sodium thiosulfate | Orphan Designation | - |
| brain ischemia | sodium nitrite | Orphan Designation | - |
| canine teeth, absence of upper permanent | Nithiodote | Orphan Designation | - |
| coccidioidomycosis | sodium nitrite | Orphan Designation | - |
| congenital secretory chloride diarrhea 1 | sodium nitrite | Orphan Designation | - |
| coronary vasospasm | sodium nitrite | Orphan Designation | - |
| cyanide poisoning | Nithiodotesodium nitrite | Orphan Designation | - |
| cyanide-induced parkinsonism | Nithiodote | Orphan Designation | - |
| dermatomyositis | sodium thiosulfate | Orphan Designation | - |
| hemolytic-uremic syndrome | sodium thiosulfate | Orphan Designation | - |
| intracranial vasospasm | sodium nitrite | Orphan Designation | - |
| ischemia reperfusion injury | sodium nitrite | Orphan Designation | - |
| non-Zellweger spectrum disorder | sodium thiosulfate | Orphan Designation | - |
| otodental syndrome | Nithiodote | Orphan Designation | - |
| platinum-induced ototoxicity | SODIUM THIOSULFATEsodium thiosulfate | Orphan Designation | FDA Approved |
| retinal ischemia | sodium nitrite | Orphan Designation | - |
| sulfur mustard poisoning | sodium thiosulfate | Orphan Designation | - |
| toxocara canis infection (canine roundworms) | Nithiodote | Orphan Designation | - |
| uremic neuropathy | sodium thiosulfate | Orphan Designation | - |
| vasa previa | sodium nitrite | Orphan Designation | - |