4
Orphan Designations
2 approved, 1 designated
0
FDA Approvals
0
Active Trials
3
Rare Diseases
across 7 areas
0
News (30d)
Quiet
Horizon Therapeutic Ireland DAC is a company with 4 orphan drug designations across 3 rare diseases.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| Friedreich ataxia | interferon gamma-1b | Des.TrialAppr. |
| chronic granulomatous disease | Actimmune | Des.TrialAppr. |
| renal cell carcinoma | Interferon gamma-1b | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
0
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
0
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
0
affecting portfolio