2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Fabry disease | lucerastat | Orphan Designation | - |
| cerebral cavernous malformation | clazosentan | Orphan Designation | - |
| coccidioidomycosis | clazosentan | Orphan Designation | - |