1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Carney-Stratakis syndrome | Small molecule kinase inhibitor | Orphan Designation | - |
| colorectal gastrointestinal stromal tumor | Small molecule kinase inhibitor | Orphan Designation | - |
| gastrointestinal stromal tumor | Small molecule kinase inhibitor | Orphan Designation | - |