1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| CBL-related disorder | Dasatinib | Orphan Designation | - |
| Noonan syndrome | Dasatinib | Orphan Designation | - |
| Noonan syndrome with multiple lentigines | Dasatinib | Orphan Designation | - |