2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| adenoid cystic carcinoma | A potent and selective inhibitor of Gamma Secretase-mediated NOTCH signaling | Orphan Designation | - |
| desmoid tumor | selective gamma secretase inhibitor of Notch-mediated signaling | Orphan Designation | - |
| familial adenomatous polyposis 1 | selective gamma secretase inhibitor of Notch-mediated signaling | Orphan Designation | - |
| tumor predisposition syndrome 3 | selective gamma secretase inhibitor of Notch-mediated signaling | Orphan Designation | - |