22
Orphan Designations
0
FDA Approvals
34
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| B-cell chronic lymphocytic leukemia | veltuzumabmilatuzumabIodine I 131 murine monoclonal antibody IgG2a to B cell | Orphan Designation | - |
| B-cell neoplasm | Iodine I 131 murine monoclonal antibody IgG2a to B cell | Orphan Designation | - |
| B-cell non-Hodgkin lymphoma | Technetium Tc99m murine monoclonal antibody (IgG2a) to B cell | Orphan Designation | - |
| B-cell prolymphocytic leukemia | Iodine I 131 murine monoclonal antibody IgG2a to B cell | Orphan Designation | - |
| Lesch-Nyhan syndrome | Iodine I 131 murine monoclonal antibody to hCG | Orphan Designation | - |
| X-linked congenital generalized hypertrichosis | Iodine I 131 murine monoclonal antibody to hCG | Orphan Designation | - |
| acute lymphoblastic leukemia | epratuzumab | Orphan Designation | - |
| acute myeloid leukemia | Antibody-drug conjugate consisting of humanized anti-HLA-DR IgG4 monoclonal antibody specific for alpha-chain linked to SN-38 via a CL2A linker | Orphan Designation | - |
| ataxia telangiectasia | Technetium Tc99m murine monoclonal antibody (IgG2a) to B cell | Orphan Designation | - |
| autoimmune thrombocytopenic purpura | veltuzumab | Orphan Designation | - |
| chromosome 1q deletion | Iodine I 123 murine monoclonal antibody to alpha-fetoprotein | Orphan Designation | - |
| familial adenomatous polyposis 1 | Iodine I 131 murine monoclonal antibody to alpha-fetoproteinIodine I 123 murine monoclonal antibody to alpha-fetoprotein | Orphan Designation | - |
| heavy chain disease | Iodine I 131 murine monoclonal antibody to hCG | Orphan Designation | - |
| hepatoblastoma | Iodine I 131 murine monoclonal antibody to alpha-fetoproteinIodine I 123 murine monoclonal antibody to alpha-fetoprotein | Orphan Designation | - |
| hepatocellular adenoma | Iodine I 131 murine monoclonal antibody to hCG | Orphan Designation | - |
| hepatocellular carcinoma | Iodine I 131 murine monoclonal antibody to alpha-fetoprotein | Orphan Designation | - |
| hypotonia-cystinuria syndrome | Iodine I 131 murine monoclonal antibody to hCG | Orphan Designation | - |
| indolent B-cell non-Hodgkin lymphoma | Technetium Tc99m murine monoclonal antibody (IgG2a) to B cell | Orphan Designation | - |
| macrotrabecular hepatoblastoma | Iodine I 131 murine monoclonal antibody to alpha-fetoproteinIodine I 123 murine monoclonal antibody to alpha-fetoprotein | Orphan Designation | - |
| malignancy diagnosed during pregnancy | Arcitumomab | Orphan Designation | - |
| malignant pancreatic neoplasm | 90Y-hPAMA4MN14 monoclonal antibody to carcinoembryonic antigen | Orphan Designation | - |
| malignant testicular germ cell tumor | Technetium Tc99m murine monoclonal antibody to hCGIodine I 131 murine monoclonal antibody to hCGIodine I 123 murine monoclonal antibody to hCG | Orphan Designation | - |
| monosomy 7 myelodysplasia and leukemia syndrome 1 | Iodine I 123 murine monoclonal antibody to alpha-fetoprotein | Orphan Designation | - |
| non-Hodgkin lymphoma | epratuzumab | Orphan Designation | - |
| ovarian carcinoma | Yttrium-90 radiolabeled humanized monoclonal anti-carcinoembroyonic antigen IgG antibody | Orphan Designation | - |
| partial deletion of chromosome 1 | Iodine I 123 murine monoclonal antibody to alpha-fetoprotein | Orphan Designation | - |
| partial deletion of the long arm of chromosome 17 | Technetium Tc99m murine monoclonal antibody to hCGTechnetium Tc99m murine monoclonal antibody to human AFPTechnetium Tc99m murine monoclonal antibody to human alpha-fetoproteinIodine I 123 murine monoclonal antibody to hCG | Orphan Designation | - |
| partial deletion of the long arm of chromosome 2 | Technetium Tc99m murine monoclonal antibody to hCGIodine I 123 murine monoclonal antibody to hCG | Orphan Designation | - |
| partial deletion of the long arm of chromosome 8 | Technetium Tc99m murine monoclonal antibody to hCGIodine I 123 murine monoclonal antibody to hCG | Orphan Designation | - |
| partial deletion of the short arm of chromosome 1 | Technetium Tc99m murine monoclonal antibody to hCGTechnetium Tc99m murine monoclonal antibody to human AFPTechnetium Tc99m murine monoclonal antibody to human alpha-fetoproteinIodine I 123 murine monoclonal antibody to hCG | Orphan Designation | - |
| partial deletion of the short arm of chromosome 11 | Technetium Tc99m murine monoclonal antibody to hCGTechnetium Tc99m murine monoclonal antibody to human AFPTechnetium Tc99m murine monoclonal antibody to human alpha-fetoproteinIodine I 123 murine monoclonal antibody to hCG | Orphan Designation | - |
| pemphigus | veltuzumab | Orphan Designation | - |
| plasma cell myeloma | milatuzumab | Orphan Designation | - |
| small cell lung carcinoma | MN14 monoclonal antibody to carcinoembryonic antigen | Orphan Designation | - |