3
Orphan Designations
0 approved, 3 designated
0
FDA Approvals
0
Active Trials
3
Rare Diseases
across 3 areas
0
News (30d)
Quiet
Imugene Limited is a company with 3 orphan drug designations across 3 rare diseases.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| adult acute lymphoblastic leukemia | allogeneic anti-CD19 chimeric antigen receptor (CAR)-T cells | Des.TrialAppr. |
| cholangiocarcinoma | Chimeric virus with a double-stranded DNA genome comprised of elements of 6 human vaccinia pox viruses with a human sodium-iodide symporter (hNIS) transgene | Des.TrialAppr. |
| mantle cell lymphoma | Allogeneic gene-edited CD19-directed CAR T cells/azercabtagene zapreleucel | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
3
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
3
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
0
affecting portfolio