2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| chronic myelogenous leukemia, BCR-ABL1 positive | Methanesulfonate-1-sec-butoxycarbonyloxymethyl-1-methyl-4-{4-[4-methyl-3-(4-pyridin-3-yl-pyrimidin-2-ylamino)-phenylcarbamoyl]-benzyl}-piperazin-1-ium | Orphan Designation | - |
| developmental and epileptic encephalopathy, 13 | imatinib mesylate | Orphan Designation | - |
| progressive multifocal leukoencephalopathy | imatinib mesylate | Orphan Designation | - |