3
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| alveolar soft part sarcoma | Pegylated Liposomal Alendronate with Doxorubicin | Orphan Designation | - |
| amyotrophic lateral sclerosis | monosialotetrahexosylganglioside | Orphan Designation | - |
| soft tissue sarcoma | doxorubicin hydrochloride encapsulated in liposomesPegylated Liposomal Alendronate with Doxorubicin | Orphan Designation | - |
| undifferentiated pleomorphic sarcoma | Pegylated Liposomal Alendronate with Doxorubicin | Orphan Designation | - |