1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| CD4+/CD56+ hematodermic neoplasm | autologous T cells transduced with lentiviral vector containing a chimeric antigen receptor directed against CD123 | Orphan Designation | - |