1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Leber congenital amaurosis 1 | riboflavin-vitamin E-TPGS topical solution | Orphan Designation | - |
| Noonan syndrome 6 | riboflavin-vitamin E-TPGS topical solution | Orphan Designation | - |
| keratoconus 1 | riboflavin-vitamin E-TPGS topical solution | Orphan Designation | - |