1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Ramos-Arroyo syndrome | recombinant human gowth hormone in an ocular delivery system | Orphan Designation | - |
| anterior segment dysgenesis 8 | recombinant human gowth hormone in an ocular delivery system | Orphan Designation | - |
| persistent hyperplastic primary vitreous, autosomal recessive | recombinant human gowth hormone in an ocular delivery system | Orphan Designation | - |