1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| myotonic dystrophy type 1 | recombinant fusion protein (biologic) made by linking human serum albumin to a human Insulin-like growth factor 2 sequence | Orphan Designation | - |