1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Beemer-Langer syndrome | PEGylated recombinant anti-Pseudomonas aeruginosa PcrV Fab' antibody | Orphan Designation | - |
| brain-lung-thyroid syndrome | PEGylated recombinant anti-Pseudomonas aeruginosa PcrV Fab' antibody | Orphan Designation | - |
| cranioectodermal dysplasia 2 | PEGylated recombinant anti-Pseudomonas aeruginosa PcrV Fab' antibody | Orphan Designation | - |